Miglustat is a medicine for Gaucher disease. As there is a link between Gaucher disease and an inherited form of Parkinson's disease I was wondering whether this drug could help PD patients with the GBA mutation. Researching this further I discovered that miglustat crossed the blood-brain barrier. So in theory miglustat could be helpful for PD patients with the GBA mutation. However, I don't find anything of a trial or test with miglustat for PD. The only thing I found was for the Niemann-Pick disease.
Does anyone know more about Miglustat trials for PD ? It is just hard for me to believe that this medicine has not been tested on PD patients with the GBA mutation.